Kalydeco is one of the first drugs that is effective at combating the root causes of a genetic disease.
Vertex Pharmaceuticals Inc.
January 2, 2013 The success of Kalydeco, a drug to treat cystic fibrosis, has been decades in the making — since the discovery of the gene associated with the disease. The time from gene discovery to successful drug may be shortening, but there are only a handful of drugs like Kalydeco on the market.
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