Gene Therapy Shows Limited, But Promising Results

Gene therapy has offered many promises of medical breakthroughs, but has kept almost none. Now, researchers report they have used gene therapy in mice to make headway against a form of muscular dystrophy. But will it work for people?


Xiao Xiao, associate professor of orthopedic surgery, molecular genetics and biochemistry at the University of Pittsburgh School of Medicine in Pittsburgh, Pa.



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