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Drug Fulfills Promise Of Research Into Cystic Fibrosis Gene

Kalydeco is one of the first drugs that is effective at combating the root causes of a genetic disease. Vertex Pharmaceuticals Inc. hide caption

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Vertex Pharmaceuticals Inc.

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Drug Fulfills Promise Of Research Into Cystic Fibrosis Gene

The success of Kalydeco, a drug to treat cystic fibrosis, has been decades in the making — since the discovery of the gene associated with the disease. The time from gene discovery to successful drug may be shortening, but there are only a handful of drugs like Kalydeco on the market.

Drug Fulfills Promise Of Research Into Cystic Fibrosis Gene

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