This image shows a brain "assembloid" consisting of two connected brain "organoids." Scientists studying these structures have restored impaired brain cells in Timothy syndrome patients. Pasca lab, Stanford University hide caption
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genetic disorders
An experimental gene therapy tested in young children with an inherited form of deafness restored some hearing for most of them. VICTOR HABBICK VISIONS/Getty Images/Science Photo Library hide caption
Gene therapy shows promise for an inherited form of deafness
Victoria Gray, who has sickle cell disease, volunteered for one of the most anticipated medical experiments in decades: the first attempt to use the gene-editing technique CRISPR to treat a genetic disorder in the United States. Meredith Rizzo/NPR hide caption
A Young Mississippi Woman's Journey Through A Pioneering Gene-Editing Experiment
Kevin Wilson's previous books include The Family Fang, Perfect Little World and Baby, You're Gonna Be Mine. Leigh Anne Couch/Ecco hide caption
For Author Kevin Wilson, Writing Offers A Brief Reprieve From Tourette's
Dieter Egli, a developmental biologist at Columbia University, and Katherine Palmerola examine a newly fertilized egg injected with a CRISPR editing tool. Rob Stein/NPR hide caption
New U.S. Experiments Aim To Create Gene-Edited Human Embryos
Jessica Morris prepares to inject a blood-clotting protein into son Landon's arm at their home in Yuba City, Calif. Heidi de Marco/Kaiser Health News hide caption
Kelly Kuhns's 2-year-old son Oliver was born with Down syndrome. She says that she was shocked when a prenatal test revealed a Trisomy 21 mutation. But, she says, "he's still a baby. He's still worthy of a life just like everybody else." Sarah McCammon/NPR hide caption