beta-thalassemia

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1st Patients To Get CRISPR Gene-Editing Treatment Continue To Thrive

Victoria Gray (second from left) with children Jamarius Wash, Jadasia Wash and Jaden Wash. Now that the gene-editing treatment has eased Gray's pain, she has been able be more active in her kids' lives and looks forward to the future. "This is really a life-changer for me," she says. Victoria Gray hide caption

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Victoria Gray

Shots - Health News

1st Patients To Get CRISPR Gene-Editing Treatment Continue To Thrive

December 15, 2020 • As the first patient to receive an experimental treatment that relied on the gene-editing technique CRISPR continues to do well 17 months later, more patients seem to be benefiting, too.

1st Patients To Get CRISPR Gene-Editing Treatment Continue To Thrive

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Gene Therapy For Inherited Blood Disorder Reduced Transfusions

Researchers used a gene-carrying virus to fix blood stem cells that were then used to treat patients with beta-thalassemia. Power and Syred/Science Photo Library/Getty Images hide caption

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Power and Syred/Science Photo Library/Getty Images

Shots - Health News

Gene Therapy For Inherited Blood Disorder Reduced Transfusions

April 18, 2018 • A small study finds promise for using gene therapy to treat patients with beta-thalassemia, a blood condition that can cause severe anemia. The experimental treatment is in early development.